From Care to Cure

Research & Development

AMT research is focused on the development of cures for rare and most of the time congenital diseases (orphan diseases).

Its research efforts will fill an unmet medical need for the treatment in the areas of metabolic disorders, ocular diseases and disorders of the central and peripheral nervous system. In addition, several pre-clinical studies are in progress, which could allow us to target selected non-orphan diseases associated with serious morbidity or high mortality caused by a genetic defect.